Presented at CDKL5 Global Patient Conference (2025)
Collaborator: Orion Pharma
Authors: Sam Amin, Carol-Anne Partridge, Helen Leonard, Jenny Downs, Helen Allvin, Valentine
Ficara, Emilie Pain, Minna A Korolainen
This study was designed to do something rare: let caregivers tell us the true story, not just through words, but through data that regulators, pharma, and policy makers will listen to
